World-renowned researchers will cover the vast Angelman syndrome research landscape, from basic research (understanding how AS works using mouse and animal models) to translational research (therapeutic development). Attendees will gain a deeper understanding of existing and emerging treatment strategies, including unsilencing approaches, downstream target rescue, gene therapy, and critical therapeutic delivery mechanisms.

The session will also provide practical guidance for families considering research participation, including what to expect in a study, participant rights, informed consent, and the safeguards in place to ensure ethical and responsible research. Families will leave with a better understanding of how to evaluate research opportunities and play an informed role in advancing Angelman syndrome research.